Disease Directory Vitamin B12- and folate-independent constitutional megaloblastic anemia
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Vitamin B12- and folate-independent constitutional megaloblastic anemia

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About Vitamin B12- and folate-independent constitutional megaloblastic anemia

Vitamin B12- and folate-independent constitutional megaloblastic anemia is a rare disease catalogued by Orphanet (ORPHA:98415). Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries worldwide.

Clinical Trial Eligibility Tips

What to know before applying to Vitamin B12- and folate-independent constitutional megaloblastic anemia trials.

Search ClinicalTrials.gov for "Vitamin B12- and folate-independent constitutional megaloblastic anemia" or Orphanet code ORPHA:98415 to find disease-specific recruiting studies.

Ask your specialist to refer you to an Orphanet-accredited Centre of Expertise for this condition.

Natural history studies and patient registries often open enrolment before drug trials — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

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Orphanet

European reference resource for rare diseases (ORPHA:98415)

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NORD

National Organization for Rare Disorders

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Find recruiting Vitamin B12- and folate-independent constitutional megaloblastic anemia trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Vitamin B12- and folate-independent constitutional megaloblastic anemia. Updated daily.