Disease Directory Thiamine-responsive megaloblastic anemia syndrome
Blood

Thiamine-responsive megaloblastic anemia syndrome

Type

Disease

Gene

SLC19A2

About Thiamine-responsive megaloblastic anemia syndrome

Thiamine-responsive megaloblastic anemia syndrome is a rare disease catalogued by Orphanet (ORPHA:49827). It is associated with the SLC19A2 gene. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Thiamine-responsive megaloblastic anemia syndrome trials.

Search ClinicalTrials.gov for "Thiamine-responsive megaloblastic anemia syndrome" or filter by Orphanet code ORPHA:49827 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

Visit website ↗

Orphanet

European reference resource for rare diseases (ORPHA:49827)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

Search NORD ↗

Find recruiting Thiamine-responsive megaloblastic anemia syndrome trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Thiamine-responsive megaloblastic anemia syndrome. Updated daily.