Disease Directory Idiopathic aplastic anemia
Blood

Idiopathic aplastic anemia

Type

Disease

Gene

PRF1, SBDS, IFNG, TERT, TERC

About Idiopathic aplastic anemia

Idiopathic aplastic anemia is a rare disease catalogued by Orphanet (ORPHA:88). It is associated with the PRF1, SBDS, IFNG genes. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Idiopathic aplastic anemia trials.

Search ClinicalTrials.gov for "Idiopathic aplastic anemia" or filter by Orphanet code ORPHA:88 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

Visit website ↗

Orphanet

European reference resource for rare diseases (ORPHA:88)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

Search NORD ↗

Find recruiting Idiopathic aplastic anemia trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Idiopathic aplastic anemia. Updated daily.