Mitochondrial

Mitochondrial disease

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studies recruiting now

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studies registered in total

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countries with a recruiting site

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recruiting study posted to date

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Recruiting trials

Fetching live from ClinicalTrials.gov. This condition is not yet in our weekly snapshot; live results only.

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Patient organisations

We do not yet list a dedicated organisation for this condition. The directories below are the best route.

A group of conditions, not a single diagnosis

Orphanet classifies “Mitochondrial disease” as a category that groups several related conditions. Trials are usually registered under the specific condition, so the figures above may undercount. Browse the conditions in this group or see the classification on Orphanet.

Treatments being studied

1 approved treatment and 11 in clinical development, from Open Targets (CC BY 4.0). Not medical advice.

Approved: Valproic Acid (Convulex)
Phase 3Ubidecarenone
Phase 3Vatiquinone
Phase 2Cysteamine Bitartrate (Cystagon)
Phase 2Bezafibrate (Bezagen xl)
Phase 2Elamipretide
Phase 2Icatibant
Phase 2Napazimone
Phase 1Acetylcysteine (A-cys)

+ 3 more in development

Related conditions

Information, not medical advice. Trial listings are shown as recorded on ClinicalTrials.gov; whether any study is right for you is a decision for you and your clinicians, and eligibility is decided by each research team. Disease information from Orphanet (CC BY 4.0).