Disease Directory Mitochondrial trifunctional protein deficiency
Mitochondrial

Mitochondrial trifunctional protein deficiency

Type

Disease

Gene

HADHA, HADHB

About Mitochondrial trifunctional protein deficiency

Mitochondrial trifunctional protein deficiency is a rare disease catalogued by Orphanet (ORPHA:746). It is associated with the HADHA, HADHB genes. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Mitochondrial trifunctional protein deficiency trials.

Search ClinicalTrials.gov for "Mitochondrial trifunctional protein deficiency" or filter by Orphanet code ORPHA:746 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

Visit website ↗

Orphanet

European reference resource for rare diseases (ORPHA:746)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

Search NORD ↗

Find recruiting Mitochondrial trifunctional protein deficiency trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Mitochondrial trifunctional protein deficiency. Updated daily.