Disease Directory Transient neonatal diabetes mellitus
Rare Disease

Transient neonatal diabetes mellitus

Type

Disease

Gene

ABCC8, KCNJ11, HYMAI, PLAGL1, ZFP57

About Transient neonatal diabetes mellitus

Transient neonatal diabetes mellitus is a rare disease catalogued by Orphanet (ORPHA:99886). It is associated with the ABCC8, KCNJ11, HYMAI genes. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Transient neonatal diabetes mellitus trials.

Search ClinicalTrials.gov for "Transient neonatal diabetes mellitus" or filter by Orphanet code ORPHA:99886 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

Visit website ↗

Orphanet

European reference resource for rare diseases (ORPHA:99886)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

Search NORD ↗

Find recruiting Transient neonatal diabetes mellitus trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Transient neonatal diabetes mellitus. Updated daily.