Neurological

Neurodegenerative syndrome due to cerebral folate transport deficiency

0

studies recruiting now

as of 7 Sept 2026

1

studies registered in total

as of 7 Sept 2026

0

countries with a recruiting site

as of 7 Sept 2026

None

recruiting study posted to date

among recruiting studies

Recruiting trials

No recruiting trial found right now.

1 study is registered for Neurodegenerative syndrome due to cerebral folate transport deficiency, but none was recruiting as of 7 Sept 2026. Here is what is still worth doing.

Keep watching

Get an email when a new Neurodegenerative syndrome due to cerebral folate transport deficiency study opens.

One email a day at most. Unsubscribe with one click.

Used only for these alerts. Privacy.

Support

Patient organisations

We do not yet list a dedicated organisation for this condition. The directories below are the best route.

About Neurodegenerative syndrome due to cerebral folate transport deficiency

RareTrial does not yet hold a plain-language description of this condition. The most reliable starting point is Orphanet’s expert page, which lists specialist centres, registries and patient organisations, and the gene involved (FOLR1).

Treatments being studied

2 approved treatments and 13 in clinical development, from Open Targets (CC BY 4.0). Not medical advice.

Approved: Flortaucipir F 18 (Tauvid)Approved: Amifampridine (Ruzurgi)
Phase 3Pimavanserin
Phase 3Fosmetpantotenate
Phase 3Latozinemab
Phase 3Posatirelin
Phase 2Peptide T
Phase 2Niacinamide (Freederm)
Phase 2Dextromethorphan
Phase 2Etazolate

+ 5 more in development

Related conditions

Information, not medical advice. Trial listings are shown as recorded on ClinicalTrials.gov; whether any study is right for you is a decision for you and your clinicians, and eligibility is decided by each research team. Disease information from Orphanet (CC BY 4.0).