Blood

Moderate hemophilia B

ORPHA:169796 ↗Gene F9Clinical subtype

5

studies recruiting now

as of 7 Sept 2026

38

studies registered in total

as of 7 Sept 2026

32

countries with a recruiting site

as of 7 Sept 2026

23 Jul 2025

most recent study posted

among recruiting studies

Recruiting trials

Showing the 5 most recently updated recruiting studies, as recorded 7 Sept 2026. Live status on each study page.

Search all Moderate hemophilia B studies

Where recruiting studies are running

Countries with at least one recruiting site among the studies above, 7 Sept 2026. Tap a country to search trials there.

Keep watching

Get an email when a new Moderate hemophilia B study opens.

One email a day at most. Unsubscribe with one click.

Used only for these alerts. Privacy.

Support

Patient organisations

We do not yet list a dedicated organisation for this condition. The directories below are the best route.

About Moderate hemophilia B

RareTrial does not yet hold a plain-language description of this condition. The most reliable starting point is Orphanet’s expert page, which lists specialist centres, registries and patient organisations, and the gene involved (F9).

Treatments being studied

13 approved treatments and 9 in clinical development, from Open Targets (CC BY 4.0). Not medical advice.

Approved: Coagulation Factor Ix Human (Coagulation factor ix human component of balfaxar)Approved: Characterised Viable Autologous Cartilage Cells Expanded Ex Vivo Expressing Specific Marker Proteins (Chondrocelect)Approved: Albutrepenonacog Alfa (Idelvion)Approved: Nonacog Beta Pegol (Refixia)Approved: Etranacogene Dezaparvovec (Hemgenix)Approved: Coagulation Factor Ix Recombinant Human (Benefix)Approved: Eptacog Beta (Activated) (Cevenfacta)Approved: Concizumab (Alhemo)Approved: Spheroids Of Human Autologous Matrix-Associated Chondrocytes (Spherox)Approved: Eftrenonacog Alfa (Alprolix)Approved: Eptacog Alfa (Activated) (Novoseven)Approved: Fidanacogene Elaparvovec (Beqvez)Approved: Marstacimab (Hympavzi)
Phase 3Anti-Inhibitor Coagulant Complex
Phase 3Trenonacog Alfa (Ixinity[tm])
Phase 3Vatreptacog Alfa (Activated)
Phase 3Fitusiran
Phase 2Bay-1093884
Phase 2Eptacog Alfa Pegol (Activated)
Phase 2Ataluren (Translarna)
Phase 1/2Verbrinacogene Setparvovec

+ 1 more in development

Related conditions

Information, not medical advice. Trial listings are shown as recorded on ClinicalTrials.gov; whether any study is right for you is a decision for you and your clinicians, and eligibility is decided by each research team. Disease information from Orphanet (CC BY 4.0).