About Late-infantile/juvenile Krabbe disease
Late-infantile/juvenile Krabbe disease is a rare disease catalogued by Orphanet (ORPHA:206443). It is associated with the GALC gene. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.
Clinical Trial Eligibility Tips
What to know before applying to Late-infantile/juvenile Krabbe disease trials.
Search ClinicalTrials.gov for "Late-infantile/juvenile Krabbe disease" or filter by Orphanet code ORPHA:206443 to find disease-specific studies.
Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.
Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.
Patient Resources
Find recruiting Late-infantile/juvenile Krabbe disease trials
Search 500,000+ studies from ClinicalTrials.gov, filtered for Late-infantile/juvenile Krabbe disease. Updated daily.