Rare condition

Familial GPIHBP1 deficiency

ORPHA:535458 ↗Gene GPIHBP1Etiological subtype

0

studies recruiting now

as of 7 Sept 2026

0

studies registered in total

as of 7 Sept 2026

0

countries with a recruiting site

as of 7 Sept 2026

None

recruiting study posted to date

among recruiting studies

Recruiting trials

No registered studies found for Familial GPIHBP1 deficiency.

ClinicalTrials.gov has no study listed under this name as of 7 Sept 2026. That can change, and there are other routes worth knowing about.

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Patient organisations

We do not yet list a dedicated organisation for this condition. The directories below are the best route.

About Familial GPIHBP1 deficiency

RareTrial does not yet hold a plain-language description of this condition. The most reliable starting point is Orphanet’s expert page, which lists specialist centres, registries and patient organisations, and the gene involved (GPIHBP1).

Treatments being studied

3 approved treatments and 4 in clinical development, from Open Targets (CC BY 4.0). Not medical advice.

Approved: Alipogene Tiparvovec (Glybera)Approved: VolanesorsenApproved: Olezarsen
Phase 3Plozasiran
Phase 2/3Cyclosporine (Capimune)
Phase 2/3Mycophenolate Mofetil (Arzip)
Phase 2Prednisolone (Cortalone)

Information, not medical advice. Trial listings are shown as recorded on ClinicalTrials.gov; whether any study is right for you is a decision for you and your clinicians, and eligibility is decided by each research team. Disease information from Orphanet (CC BY 4.0).