RecruitingPhase 3NCT06302348
30
studies recruiting now
as of 7 Sept 2026
172
studies registered in total
as of 7 Sept 2026
6
countries with a recruiting site
as of 7 Sept 2026
10 Jul 2026
most recent study posted
among recruiting studies
Recruiting trials
RecruitingPhase 1NCT07241234
A Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AG-181 in Subjects With Phenylketonuria
RecruitingNCT07551921
PheCheck™ Validation Study
RecruitingPhase 2NCT07694440
A Study of MZE782 in Adults With PKU
RecruitingPhase 1 / Phase 2NCT06332807
AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)
Showing the 5 most recently updated recruiting studies, as recorded 7 Sept 2026. Live status on each study page.
See all 30 recruiting studiesWhere recruiting studies are running
Countries with at least one recruiting site among the studies above, 7 Sept 2026. Tap a country to search trials there.
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Patient organisations
We do not yet list a dedicated organisation for this condition. The directories below are the best route.
About Classic phenylketonuria
RareTrial does not yet hold a plain-language description of this condition. The most reliable starting point is Orphanet’s expert page, which lists specialist centres, registries and patient organisations.
Treatments being studied
4 approved treatments and 3 in clinical development, from Open Targets (CC BY 4.0). Not medical advice.
Approved: Sapropterin Dihydrochloride (Kuvan)Approved: SapropterinApproved: SepiapterinApproved: Pegvaliase (Palynziq)
Phase 3Labafenogene Marselecobac
Phase 1/2Bevufenogene Nofeparvovec
Phase 1Moxifloxacin (Avelox)
Related conditions
Information, not medical advice. Trial listings are shown as recorded on ClinicalTrials.gov; whether any study is right for you is a decision for you and your clinicians, and eligibility is decided by each research team. Disease information from Orphanet (CC BY 4.0).