Disease Directory Autosomal recessive distal myopathy
Neuromuscular

Autosomal recessive distal myopathy

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Category

About Autosomal recessive distal myopathy

Autosomal recessive distal myopathy is a rare disease catalogued by Orphanet (ORPHA:206653). Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries worldwide.

Clinical Trial Eligibility Tips

What to know before applying to Autosomal recessive distal myopathy trials.

Search ClinicalTrials.gov for "Autosomal recessive distal myopathy" or Orphanet code ORPHA:206653 to find disease-specific recruiting studies.

Ask your specialist to refer you to an Orphanet-accredited Centre of Expertise for this condition.

Natural history studies and patient registries often open enrolment before drug trials — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

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Orphanet

European reference resource for rare diseases (ORPHA:206653)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

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Find recruiting Autosomal recessive distal myopathy trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Autosomal recessive distal myopathy. Updated daily.