Blood

Acute mast cell leukemia

ORPHA:566393 ↗Gene KITClinical subtype

4

studies recruiting now

as of 7 Sept 2026

67

studies registered in total

as of 7 Sept 2026

14

countries with a recruiting site

as of 7 Sept 2026

9 Apr 2024

most recent study posted

among recruiting studies

Recruiting trials

Showing the 4 most recently updated recruiting studies, as recorded 7 Sept 2026. Live status on each study page.

Search all Acute mast cell leukemia studies

Where recruiting studies are running

Countries with at least one recruiting site among the studies above, 7 Sept 2026. Tap a country to search trials there.

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Patient organisations

We do not yet list a dedicated organisation for this condition. The directories below are the best route.

About Acute mast cell leukemia

RareTrial does not yet hold a plain-language description of this condition. The most reliable starting point is Orphanet’s expert page, which lists specialist centres, registries and patient organisations, and the gene involved (KIT).

Treatments being studied

17 approved treatments and 82 in clinical development, from Open Targets (CC BY 4.0). Not medical advice.

Approved: Clofarabine (Clolar)Approved: Pegaspargase (Oncaspar)Approved: Calaspargase Pegol (Asparlas)Approved: Blinatumomab (Blincyto)Approved: Dasatinib Anhydrous (Dasatinib accord)Approved: Asparaginase Erwinia Chrysanthemi (Erwinase[r] erwinaze[tm])Approved: Cytarabine (Alexan)Approved: Crisantaspase (Enrylaze)Approved: Chlorambucil (Leukeran)Approved: Mercaptopurine (Mercaptopurine)Approved: Ponatinib Hydrochloride (Iclusig)Approved: Methotrexate (Ebetrex)Approved: Plerixafor (Mozobil)Approved: Inotuzumab Ozogamicin (Besponsa)Approved: Rituximab (Blitzima)Approved: Dasatinib (Dasatinib accord healthcare)Approved: Thioguanine (Lanvis)
Phase 3Vincristine Sulfate (Leurocristine sulfate)
Phase 3Cyclophosphamide (Cyclophosphamide)
Phase 3Mitoxantrone
Phase 3Doxorubicin (Adriblastina)
Phase 3Leucovorin Calcium (Leucovorin calcium)
Phase 3Interferon Alfa-2a (Alpheon)
Phase 3Vincristine
Phase 3Epirubicin Hydrochloride (Ellence)

+ 74 more in development

Related conditions

Information, not medical advice. Trial listings are shown as recorded on ClinicalTrials.gov; whether any study is right for you is a decision for you and your clinicians, and eligibility is decided by each research team. Disease information from Orphanet (CC BY 4.0).