Disease Directory Very long chain acyl-CoA dehydrogenase deficiency
Rare Disease

Very long chain acyl-CoA dehydrogenase deficiency

Type

Disease

Gene

ACADVL

About Very long chain acyl-CoA dehydrogenase deficiency

Very long chain acyl-CoA dehydrogenase deficiency is a rare disease catalogued by Orphanet (ORPHA:26793). It is associated with the ACADVL gene. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Very long chain acyl-CoA dehydrogenase deficiency trials.

Search ClinicalTrials.gov for "Very long chain acyl-CoA dehydrogenase deficiency" or filter by Orphanet code ORPHA:26793 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

Visit website ↗

Orphanet

European reference resource for rare diseases (ORPHA:26793)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

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Find recruiting Very long chain acyl-CoA dehydrogenase deficiency trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Very long chain acyl-CoA dehydrogenase deficiency. Updated daily.