Disease Directory Severe X-linked mitochondrial encephalomyopathy
Neuromuscular

Severe X-linked mitochondrial encephalomyopathy

Type

Disease

Gene

AIFM1

About Severe X-linked mitochondrial encephalomyopathy

Severe X-linked mitochondrial encephalomyopathy is a rare disease catalogued by Orphanet (ORPHA:238329). It is associated with the AIFM1 gene. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Severe X-linked mitochondrial encephalomyopathy trials.

Search ClinicalTrials.gov for "Severe X-linked mitochondrial encephalomyopathy" or filter by Orphanet code ORPHA:238329 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

Visit website ↗

Orphanet

European reference resource for rare diseases (ORPHA:238329)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

Search NORD ↗

Find recruiting Severe X-linked mitochondrial encephalomyopathy trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Severe X-linked mitochondrial encephalomyopathy. Updated daily.