Disease Directory SETD2-related microcephaly-severe intellectual disability-multiple congenital anomalies syndrome
Rare Disease

SETD2-related microcephaly-severe intellectual disability-multiple congenital anomalies syndrome

Type

Malformation syndrome

Gene

SETD2

About SETD2-related microcephaly-severe intellectual disability-multiple congenital anomalies syndrome

SETD2-related microcephaly-severe intellectual disability-multiple congenital anomalies syndrome is a rare disease catalogued by Orphanet (ORPHA:597743). It is associated with the SETD2 gene. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to SETD2-related microcephaly-severe intellectual disability-multiple congenital anomalies syndrome trials.

Search ClinicalTrials.gov for "SETD2-related microcephaly-severe intellectual disability-multiple congenital anomalies syndrome" or filter by Orphanet code ORPHA:597743 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

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Orphanet

European reference resource for rare diseases (ORPHA:597743)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

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Find recruiting SETD2-related microcephaly-severe intellectual disability-multiple congenital anomalies syndrome trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for SETD2-related microcephaly-severe intellectual disability-multiple congenital anomalies syndrome. Updated daily.