Disease Directory Radio-ulnar synostosis-amegakaryocytic thrombocytopenia syndrome
Blood

Radio-ulnar synostosis-amegakaryocytic thrombocytopenia syndrome

Type

Malformation syndrome

Gene

MECOM, HOXA11

About Radio-ulnar synostosis-amegakaryocytic thrombocytopenia syndrome

Radio-ulnar synostosis-amegakaryocytic thrombocytopenia syndrome is a rare disease catalogued by Orphanet (ORPHA:71289). It is associated with the MECOM, HOXA11 genes. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Radio-ulnar synostosis-amegakaryocytic thrombocytopenia syndrome trials.

Search ClinicalTrials.gov for "Radio-ulnar synostosis-amegakaryocytic thrombocytopenia syndrome" or filter by Orphanet code ORPHA:71289 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

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Orphanet

European reference resource for rare diseases (ORPHA:71289)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

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Find recruiting Radio-ulnar synostosis-amegakaryocytic thrombocytopenia syndrome trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Radio-ulnar synostosis-amegakaryocytic thrombocytopenia syndrome. Updated daily.