Disease Directory Progressive muscular atrophy
Rare Disease

Progressive muscular atrophy

Type

Disease

About Progressive muscular atrophy

Progressive muscular atrophy is a rare disease catalogued by Orphanet (ORPHA:454706). Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries worldwide.

Clinical Trial Eligibility Tips

What to know before applying to Progressive muscular atrophy trials.

Search ClinicalTrials.gov for "Progressive muscular atrophy" or Orphanet code ORPHA:454706 to find disease-specific recruiting studies.

Ask your specialist to refer you to an Orphanet-accredited Centre of Expertise for this condition.

Natural history studies and patient registries often open enrolment before drug trials — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

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Orphanet

European reference resource for rare diseases (ORPHA:454706)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

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Find recruiting Progressive muscular atrophy trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Progressive muscular atrophy. Updated daily.