Disease Directory Posterior-predominant lissencephaly-broad flat pons and medulla-midline crossing defects syndrome
Neurological

Posterior-predominant lissencephaly-broad flat pons and medulla-midline crossing defects syndrome

Type

Malformation syndrome

Gene

MACF1, CEP85L

About Posterior-predominant lissencephaly-broad flat pons and medulla-midline crossing defects syndrome

Posterior-predominant lissencephaly-broad flat pons and medulla-midline crossing defects syndrome is a rare disease catalogued by Orphanet (ORPHA:572013). It is associated with the MACF1, CEP85L genes. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Posterior-predominant lissencephaly-broad flat pons and medulla-midline crossing defects syndrome trials.

Search ClinicalTrials.gov for "Posterior-predominant lissencephaly-broad flat pons and medulla-midline crossing defects syndrome" or filter by Orphanet code ORPHA:572013 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

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Orphanet

European reference resource for rare diseases (ORPHA:572013)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

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Find recruiting Posterior-predominant lissencephaly-broad flat pons and medulla-midline crossing defects syndrome trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Posterior-predominant lissencephaly-broad flat pons and medulla-midline crossing defects syndrome. Updated daily.