Disease Directory Pelizaeus-Merzbacher disease, connatal form
Rare Disease

Pelizaeus-Merzbacher disease, connatal form

Type

Clinical subtype

Gene

PLP1

About Pelizaeus-Merzbacher disease, connatal form

Pelizaeus-Merzbacher disease, connatal form is a rare disease catalogued by Orphanet (ORPHA:280210). It is associated with the PLP1 gene. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Pelizaeus-Merzbacher disease, connatal form trials.

Search ClinicalTrials.gov for "Pelizaeus-Merzbacher disease, connatal form" or filter by Orphanet code ORPHA:280210 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

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Orphanet

European reference resource for rare diseases (ORPHA:280210)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

Search NORD ↗

Find recruiting Pelizaeus-Merzbacher disease, connatal form trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Pelizaeus-Merzbacher disease, connatal form. Updated daily.