Disease Directory Marfanoid habitus-facial dysmorphism-skeletal abnormality-heart defect syndrome
Connective Tissue

Marfanoid habitus-facial dysmorphism-skeletal abnormality-heart defect syndrome

Type

Disease

Gene

ABL1

About Marfanoid habitus-facial dysmorphism-skeletal abnormality-heart defect syndrome

Marfanoid habitus-facial dysmorphism-skeletal abnormality-heart defect syndrome is a rare disease catalogued by Orphanet (ORPHA:643503). It is associated with the ABL1 gene. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Marfanoid habitus-facial dysmorphism-skeletal abnormality-heart defect syndrome trials.

Search ClinicalTrials.gov for "Marfanoid habitus-facial dysmorphism-skeletal abnormality-heart defect syndrome" or filter by Orphanet code ORPHA:643503 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

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Orphanet

European reference resource for rare diseases (ORPHA:643503)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

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Find recruiting Marfanoid habitus-facial dysmorphism-skeletal abnormality-heart defect syndrome trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Marfanoid habitus-facial dysmorphism-skeletal abnormality-heart defect syndrome. Updated daily.