Disease Directory Lissencephaly due to LIS1 mutation
Neurological

Lissencephaly due to LIS1 mutation

Type

Disease

Gene

PAFAH1B1

About Lissencephaly due to LIS1 mutation

Lissencephaly due to LIS1 mutation is a rare disease catalogued by Orphanet (ORPHA:95232). It is associated with the PAFAH1B1 gene. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Lissencephaly due to LIS1 mutation trials.

Search ClinicalTrials.gov for "Lissencephaly due to LIS1 mutation" or filter by Orphanet code ORPHA:95232 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

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Orphanet

European reference resource for rare diseases (ORPHA:95232)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

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Find recruiting Lissencephaly due to LIS1 mutation trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Lissencephaly due to LIS1 mutation. Updated daily.