Disease Directory Lenz-Majewski hyperostotic dysplasia
Rare Disease

Lenz-Majewski hyperostotic dysplasia

Type

Malformation syndrome

Gene

PTDSS1

About Lenz-Majewski hyperostotic dysplasia

Lenz-Majewski hyperostotic dysplasia is a rare disease catalogued by Orphanet (ORPHA:2658). It is associated with the PTDSS1 gene. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Lenz-Majewski hyperostotic dysplasia trials.

Search ClinicalTrials.gov for "Lenz-Majewski hyperostotic dysplasia" or filter by Orphanet code ORPHA:2658 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

Visit website ↗

Orphanet

European reference resource for rare diseases (ORPHA:2658)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

Search NORD ↗

Find recruiting Lenz-Majewski hyperostotic dysplasia trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Lenz-Majewski hyperostotic dysplasia. Updated daily.