Respiratory

Hereditary pulmonary alveolar proteinosis

2

studies recruiting now

as of 7 Sept 2026

4

studies registered in total

as of 7 Sept 2026

4

countries with a recruiting site

as of 7 Sept 2026

9 Mar 2023

most recent study posted

among recruiting studies

Recruiting trials

RecruitingPhase 1 / Phase 2NCT05761899

Safety and Efficacy of PMT Therapy of hPAP

Sponsor Children's Hospital Medical Center, CincinnatiWhere United States (1 site)Studying Gene-Corrected Macrophages administered by bronchoscopic instillationUpdated 19 Dec 2025

Showing the 2 most recently updated recruiting studies, as recorded 7 Sept 2026. Live status on each study page.

Search all Hereditary pulmonary alveolar proteinosis studies

Where recruiting studies are running

Countries with at least one recruiting site among the studies above, 7 Sept 2026. Tap a country to search trials there.

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Patient organisations

We do not yet list a dedicated organisation for this condition. The directories below are the best route.

About Hereditary pulmonary alveolar proteinosis

RareTrial does not yet hold a plain-language description of this condition. The most reliable starting point is Orphanet’s expert page, which lists specialist centres, registries and patient organisations, and the genes involved (CSF2RB, CSF2RA).

Treatments being studied

1 in clinical development, from Open Targets (CC BY 4.0). Not medical advice.

Phase 2Sargramostim (Leukine)

Related conditions

Information, not medical advice. Trial listings are shown as recorded on ClinicalTrials.gov; whether any study is right for you is a decision for you and your clinicians, and eligibility is decided by each research team. Disease information from Orphanet (CC BY 4.0).