Disease Directory Hereditary combined deficiency of vitamin K-dependent clotting factors
Rare Disease

Hereditary combined deficiency of vitamin K-dependent clotting factors

Type

Disease

Gene

GGCX, VKORC1

About Hereditary combined deficiency of vitamin K-dependent clotting factors

Hereditary combined deficiency of vitamin K-dependent clotting factors is a rare disease catalogued by Orphanet (ORPHA:98434). It is associated with the GGCX, VKORC1 genes. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Hereditary combined deficiency of vitamin K-dependent clotting factors trials.

Search ClinicalTrials.gov for "Hereditary combined deficiency of vitamin K-dependent clotting factors" or filter by Orphanet code ORPHA:98434 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

Visit website ↗

Orphanet

European reference resource for rare diseases (ORPHA:98434)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

Search NORD ↗

Find recruiting Hereditary combined deficiency of vitamin K-dependent clotting factors trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Hereditary combined deficiency of vitamin K-dependent clotting factors. Updated daily.