Disease Directory GMPPB-related limb-girdle muscular dystrophy R19
Neuromuscular

GMPPB-related limb-girdle muscular dystrophy R19

Type

Disease

Gene

GMPPB

About GMPPB-related limb-girdle muscular dystrophy R19

GMPPB-related limb-girdle muscular dystrophy R19 is a rare disease catalogued by Orphanet (ORPHA:363623). It is associated with the GMPPB gene. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to GMPPB-related limb-girdle muscular dystrophy R19 trials.

Search ClinicalTrials.gov for "GMPPB-related limb-girdle muscular dystrophy R19" or filter by Orphanet code ORPHA:363623 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

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Orphanet

European reference resource for rare diseases (ORPHA:363623)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

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Find recruiting GMPPB-related limb-girdle muscular dystrophy R19 trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for GMPPB-related limb-girdle muscular dystrophy R19. Updated daily.