Disease Directory GM3 synthase deficiency
Rare Disease

GM3 synthase deficiency

Type

Disease

Gene

ST3GAL5

About GM3 synthase deficiency

GM3 synthase deficiency is a rare disease catalogued by Orphanet (ORPHA:370933). It is associated with the ST3GAL5 gene. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to GM3 synthase deficiency trials.

Search ClinicalTrials.gov for "GM3 synthase deficiency" or filter by Orphanet code ORPHA:370933 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

Visit website ↗

Orphanet

European reference resource for rare diseases (ORPHA:370933)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

Search NORD ↗

Find recruiting GM3 synthase deficiency trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for GM3 synthase deficiency. Updated daily.