About GM1 gangliosidosis type 1
GM1 gangliosidosis type 1 is a rare disease catalogued by Orphanet (ORPHA:79255). It is associated with the GLB1 gene. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.
Clinical Trial Eligibility Tips
What to know before applying to GM1 gangliosidosis type 1 trials.
Search ClinicalTrials.gov for "GM1 gangliosidosis type 1" or filter by Orphanet code ORPHA:79255 to find disease-specific studies.
Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.
Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.
Patient Resources
Find recruiting GM1 gangliosidosis type 1 trials
Search 500,000+ studies from ClinicalTrials.gov, filtered for GM1 gangliosidosis type 1. Updated daily.