Disease Directory Familial platelet disorder with associated myeloid malignancy
Blood

Familial platelet disorder with associated myeloid malignancy

Type

Disease

Gene

RUNX1

About Familial platelet disorder with associated myeloid malignancy

Familial platelet disorder with associated myeloid malignancy is a rare disease catalogued by Orphanet (ORPHA:71290). It is associated with the RUNX1 gene. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Familial platelet disorder with associated myeloid malignancy trials.

Search ClinicalTrials.gov for "Familial platelet disorder with associated myeloid malignancy" or filter by Orphanet code ORPHA:71290 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

Visit website ↗

Orphanet

European reference resource for rare diseases (ORPHA:71290)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

Search NORD ↗

Find recruiting Familial platelet disorder with associated myeloid malignancy trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Familial platelet disorder with associated myeloid malignancy. Updated daily.