Disease Directory Familial isolated dilated cardiomyopathy
Neuromuscular

Familial isolated dilated cardiomyopathy

Type

Disease

Gene

TAF1A, GET3, VEZF1, RPL3L, MYBPC3, JPH2

About Familial isolated dilated cardiomyopathy

Familial isolated dilated cardiomyopathy is a rare disease catalogued by Orphanet (ORPHA:154). It is associated with the TAF1A, GET3, VEZF1 genes. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Familial isolated dilated cardiomyopathy trials.

Search ClinicalTrials.gov for "Familial isolated dilated cardiomyopathy" or filter by Orphanet code ORPHA:154 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

Visit website ↗

Orphanet

European reference resource for rare diseases (ORPHA:154)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

Search NORD ↗

Find recruiting Familial isolated dilated cardiomyopathy trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Familial isolated dilated cardiomyopathy. Updated daily.