Disease Directory Familial infantile bilateral striatal necrosis
Rare Disease

Familial infantile bilateral striatal necrosis

Type

Disease

Gene

NUP54, ADAR, MT-ATP6, NUP62

About Familial infantile bilateral striatal necrosis

Familial infantile bilateral striatal necrosis is a rare disease catalogued by Orphanet (ORPHA:225154). It is associated with the NUP54, ADAR, MT-ATP6 genes. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Familial infantile bilateral striatal necrosis trials.

Search ClinicalTrials.gov for "Familial infantile bilateral striatal necrosis" or filter by Orphanet code ORPHA:225154 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

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Orphanet

European reference resource for rare diseases (ORPHA:225154)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

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Find recruiting Familial infantile bilateral striatal necrosis trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Familial infantile bilateral striatal necrosis. Updated daily.