Disease Directory Dyskeratosis congenita
Rare Disease

Dyskeratosis congenita

Type

Disease

Gene

NPM1, DKC1, TERT, TERC, TINF2, NOP10

About Dyskeratosis congenita

Dyskeratosis congenita is a rare disease catalogued by Orphanet (ORPHA:1775). It is associated with the NPM1, DKC1, TERT genes. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Dyskeratosis congenita trials.

Search ClinicalTrials.gov for "Dyskeratosis congenita" or filter by Orphanet code ORPHA:1775 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

Visit website ↗

Orphanet

European reference resource for rare diseases (ORPHA:1775)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

Search NORD ↗

Find recruiting Dyskeratosis congenita trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Dyskeratosis congenita. Updated daily.