About Congenital thrombotic thrombocytopenic purpura
Congenital thrombotic thrombocytopenic purpura is a rare disease catalogued by Orphanet (ORPHA:93583). It is associated with the ADAMTS13 gene. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.
Clinical Trial Eligibility Tips
What to know before applying to Congenital thrombotic thrombocytopenic purpura trials.
Search ClinicalTrials.gov for "Congenital thrombotic thrombocytopenic purpura" or filter by Orphanet code ORPHA:93583 to find disease-specific studies.
Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.
Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.
Patient Resources
Find recruiting Congenital thrombotic thrombocytopenic purpura trials
Search 500,000+ studies from ClinicalTrials.gov, filtered for Congenital thrombotic thrombocytopenic purpura. Updated daily.