Disease Directory Congenital fibrosis of extraocular muscles
Rare Disease

Congenital fibrosis of extraocular muscles

Type

Disease

Gene

COL25A1, TUBA1A, PHOX2A, KIF21A, TUBB3, TUBB2B

About Congenital fibrosis of extraocular muscles

Congenital fibrosis of extraocular muscles is a rare disease catalogued by Orphanet (ORPHA:45358). It is associated with the COL25A1, TUBA1A, PHOX2A genes. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Congenital fibrosis of extraocular muscles trials.

Search ClinicalTrials.gov for "Congenital fibrosis of extraocular muscles" or filter by Orphanet code ORPHA:45358 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

Visit website ↗

Orphanet

European reference resource for rare diseases (ORPHA:45358)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

Search NORD ↗

Find recruiting Congenital fibrosis of extraocular muscles trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Congenital fibrosis of extraocular muscles. Updated daily.