Disease Directory Autosomal dominant severe congenital neutropenia
Blood

Autosomal dominant severe congenital neutropenia

Type

Disease

Gene

TCIRG1, ELANE, GFI1, CLPB, SRP19

About Autosomal dominant severe congenital neutropenia

Autosomal dominant severe congenital neutropenia is a rare disease catalogued by Orphanet (ORPHA:486). It is associated with the TCIRG1, ELANE, GFI1 genes. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Autosomal dominant severe congenital neutropenia trials.

Search ClinicalTrials.gov for "Autosomal dominant severe congenital neutropenia" or filter by Orphanet code ORPHA:486 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

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Orphanet

European reference resource for rare diseases (ORPHA:486)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

Search NORD ↗

Find recruiting Autosomal dominant severe congenital neutropenia trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Autosomal dominant severe congenital neutropenia. Updated daily.