Disease Directory Autosomal dominant limb-girdle muscular dystrophy type 1C
Neuromuscular

Autosomal dominant limb-girdle muscular dystrophy type 1C

Type

Disease

About Autosomal dominant limb-girdle muscular dystrophy type 1C

Autosomal dominant limb-girdle muscular dystrophy type 1C is a rare disease catalogued by Orphanet (ORPHA:265). Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries worldwide.

Clinical Trial Eligibility Tips

What to know before applying to Autosomal dominant limb-girdle muscular dystrophy type 1C trials.

Search ClinicalTrials.gov for "Autosomal dominant limb-girdle muscular dystrophy type 1C" or Orphanet code ORPHA:265 to find disease-specific recruiting studies.

Ask your specialist to refer you to an Orphanet-accredited Centre of Expertise for this condition.

Natural history studies and patient registries often open enrolment before drug trials — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

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Orphanet

European reference resource for rare diseases (ORPHA:265)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

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Find recruiting Autosomal dominant limb-girdle muscular dystrophy type 1C trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Autosomal dominant limb-girdle muscular dystrophy type 1C. Updated daily.