Disease Directory Alpha-thalassemia-myelodysplastic syndrome
Blood

Alpha-thalassemia-myelodysplastic syndrome

Type

Disease

Gene

ATRX

About Alpha-thalassemia-myelodysplastic syndrome

Alpha-thalassemia-myelodysplastic syndrome is a rare disease catalogued by Orphanet (ORPHA:231401). It is associated with the ATRX gene. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Alpha-thalassemia-myelodysplastic syndrome trials.

Search ClinicalTrials.gov for "Alpha-thalassemia-myelodysplastic syndrome" or filter by Orphanet code ORPHA:231401 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

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Orphanet

European reference resource for rare diseases (ORPHA:231401)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

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Find recruiting Alpha-thalassemia-myelodysplastic syndrome trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Alpha-thalassemia-myelodysplastic syndrome. Updated daily.