About Aicardi-Goutières syndrome
Aicardi-Goutières syndrome is a rare disease catalogued by Orphanet (ORPHA:51). It is associated with the LSM11, RNU7-1, SAMHD1 genes. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.
Clinical Trial Eligibility Tips
What to know before applying to Aicardi-Goutières syndrome trials.
Search ClinicalTrials.gov for "Aicardi-Goutières syndrome" or filter by Orphanet code ORPHA:51 to find disease-specific studies.
Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.
Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.
Patient Resources
Find recruiting Aicardi-Goutières syndrome trials
Search 500,000+ studies from ClinicalTrials.gov, filtered for Aicardi-Goutières syndrome. Updated daily.