Disease Directory Adult-onset dystonia-parkinsonism
Neurological

Adult-onset dystonia-parkinsonism

Type

Disease

Gene

PLA2G6

About Adult-onset dystonia-parkinsonism

Adult-onset dystonia-parkinsonism is a rare disease catalogued by Orphanet (ORPHA:199351). It is associated with the PLA2G6 gene. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Adult-onset dystonia-parkinsonism trials.

Search ClinicalTrials.gov for "Adult-onset dystonia-parkinsonism" or filter by Orphanet code ORPHA:199351 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

Visit website ↗

Orphanet

European reference resource for rare diseases (ORPHA:199351)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

Search NORD ↗

Find recruiting Adult-onset dystonia-parkinsonism trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Adult-onset dystonia-parkinsonism. Updated daily.