Disease Directory Acute megakaryoblastic leukemia in children with Down syndrome
Blood

Acute megakaryoblastic leukemia in children with Down syndrome

Type

Clinical subtype

Gene

GATA1

About Acute megakaryoblastic leukemia in children with Down syndrome

Acute megakaryoblastic leukemia in children with Down syndrome is a rare disease catalogued by Orphanet (ORPHA:99887). It is associated with the GATA1 gene. Search below for active recruiting clinical trials from ClinicalTrials.gov, or visit the Orphanet expert page for specialist centres, natural history studies, and patient registries.

Clinical Trial Eligibility Tips

What to know before applying to Acute megakaryoblastic leukemia in children with Down syndrome trials.

Search ClinicalTrials.gov for "Acute megakaryoblastic leukemia in children with Down syndrome" or filter by Orphanet code ORPHA:99887 to find disease-specific studies.

Ask your specialist to refer you to a Centre of Expertise — Orphanet lists all accredited centres for this condition worldwide.

Natural history studies and patient registries often enrol before drug trials open — contact the Orphanet patient community first.

Patient Resources

Patient Organization

Orphanet

Visit website ↗

Orphanet

European reference resource for rare diseases (ORPHA:99887)

View on Orphanet ↗

NORD

National Organization for Rare Disorders

Search NORD ↗

Find recruiting Acute megakaryoblastic leukemia in children with Down syndrome trials

Search 500,000+ studies from ClinicalTrials.gov, filtered for Acute megakaryoblastic leukemia in children with Down syndrome. Updated daily.